)
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Panel Discussion: Accelerating Ultra-Personalised Therapies for Rare Genetic Diseases: From Diagnosis to Delivery
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Addressing the fragmented system
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Navigating regulatory pathways for single-patient therapies
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Accelerating diagnosis-to-treatment timelines
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Establishing a coordinated roadmap for licensing, reimbursement, and NHS delivery
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Engaging stakeholders and patient advocacy groups
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Ensuring patient-centric approaches in therapy development
